Category Archives: Gene Therapy

Case study: Challenges of ultra-orphan drug development: Glybera, a gene therapy for LPL deficiency – Video


01-02-2012 05:24 What were the significant challenges faced during ultra-orphan drug development? How were clinical trials adapted to demonstrate the purpose of the treatment? Continue reading

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'Goldilocks' gene could determine best treatment for TB patients

( King's College London ) Tuberculosis patients may receive treatments in the future according to what version they have of a single 'Goldilocks' gene, says an international research team from Oxford University, King's College London, Vietnam and the USA.Source:http://news.search.yahoo.com/news/rss?p=gene+medicine&ei=UTF-8&fl=0&x=wrt

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Entering into the clinic with an intracerebral gene therapy product / Karen Aiach, Project Manager, – Video


01-02-2012 05:22 Specific challenges of avant-garde therapies Authorities/sponsors: being concomitantly on a learning curve Translational research: key success factors Case study: SAF-301 Continue reading

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UPDATE 2-Shire partners Sangamo in gene therapy for hemophilia

* Shire to pay $13 mln upfront, plus milestones * Sangamo shares rise more than 25 percent (Adds analyst comment, share price) Feb 1 (Reuters) – Pharmaceutical company Shire said on Wednesday it would … Continue reading

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Apes Trailer/Gene Therapy – Video


26-01-2012 21:26 Short Trailer on the history and applications of Gene Therapy in the modern medical scene. Written and directed by Thenmozhi Soundaranagaran Score by Keith Jackson Continue reading

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Gene Therapy: Dr. Zehhr – Video


23-01-2012 19:59 For Bio Honors Continue reading

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Amsterdam Molecular Therapeutics Announces European Commission Delays Decision on Glybera® Marketing Authorisation and …

AMSTERDAM, January 30, 2012 /PRNewswire/ –Amsterdam Molecular Therapeutics (Euronext: AMT – News), a leader in the field of human gene therapy, was informed on Friday January 27, 2012 after business hours that … Continue reading

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Gene therapy is a 'disruptive science' ready for commercial development

The time for commercial development of gene therapy has come. Patients with diseases treatable and curable with gene therapy deserve access to the technology, which has demonstrated both its effectiveness and feasibility, says James Wilson, MD, PhD, Editor-in-Chief of Human … Continue reading

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Rivals see no need to match Roche's big gene bet

DAVOS, Switzerland (Reuters) – Roche Holding AG's rivals Sanofi SA and Novartis AG see no need to match the Swiss drug maker in buying a gene-decoding business like Illumina Inc and reckon they can do partnerships instead. The relaxed attitude … Continue reading

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James Wilson, MD, Ph.D., on Gene Therapy as a Disruptive Technology – Video


20-01-2012 17:36 Dr. Continue reading

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Penn researchers report gain in using gene therapy to battle blindness

Four years ago, teams of researchers at the University of Pennsylvania and elsewhere made headlines by restoring some sight to blind people, though it was a form of blindness few had heard of. Continue reading

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Gene therapy is a 'disruptive science' ready for commercial development

The time for commercial development of gene therapy has come. Patients with diseases treatable and curable with gene therapy deserve access to the technology, which has demonstrated both its effectiveness and feasibility, says James Wilson, MD, PhD, Editor-in-Chief of Human Gene Therapy in a provocative commentary and accompanying videocast Continue reading

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The key to gene therapy in the HIV virus – Video


20-01-2012 04:30 www.telethon.it – Luigi Naldini is the director of the San Raffaele-Telethon Institute for Gene Therapy (HSR-TIGET) in Milan. He is considered one of the greatest experts in the world on gene therapy Continue reading

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Progressus Therapy Appoints Gene Clark CEO

Company Receives Additional Investment from Sterling Partners to Strengthen and Expand Role as a Lea… Continue reading

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Gene therapy, a totally Italian success – Video


16-01-2012 03:57 www.telethon.it – Gene therapy is the technique that allows the prevention and treatment of diseases thanks to DNA transfer. Continue reading

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MSC-mediated RNAi transfer holds promise for Huntington's disease

A team of researchers at the UC Davis Institute for Regenerative Cures has developed a technique for using stem cells to deliver therapy that specifically targets the genetic abnormality found in Huntington's disease, a hereditary brain disorder that causes progressive uncontrolled movements, dementia and death. Continue reading

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Progressus Therapy Appoints New Leadership Team

TAMPA, Fla., Jan. 20, 2012 /PRNewswire/ – Progressus Therapy, a leading provider of special education solutions to school districts and communities around the country, announced that it has appointed … Continue reading

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Promega announces beta launch of Find My Gene

Promega announces the beta launch of the online gene exploration tool Find My Gene. Find My Gene integrates a number of robust functionalities to help researchers better understand their gene's function. Continue reading

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UC Davis investigators achieve important step toward treating Huntington's disease

( University of California – Davis Health System ) A team of researchers at the UC Davis Institute for Regenerative Cures has developed a technique for using stem cells to deliver therapy that specifically targets the genetic abnormality found in Huntington's disease, a hereditary brain disorder that causes progressive uncontrolled movements, dementia and death. Continue reading

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Gene variant 'prostate cancer link'

Men who inherit a rare genetic mutation are 10 to 20 times more likely than average to develop prostate cancer, a study has found.Source:http://news.search.yahoo.com/news/rss?p=gene+medicine&ei=UTF-8&fl=0&x=wrt

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